Total number of Results for c.8163G>A,c.52CAG(36_39) are 6
ASPsiRNA ID Pairing of target region (top) and ASP-siRNA (bottom) Efficacy (mut)(%) Efficacy (wt) (%) Diff Gene Disease Mutation RefSNP Analysis Pubmed ID
ASPsiRNA ID Mutant allele/ASP-siRNA Efficacy
for mutant(%)
Efficacy
for wild (%)
Relative Difference (%) Gene Disease Mutation RefSNP Analysis Pubmed ID
aspsirna0053 GUUUGAGCUGAUGUAUGUG
CAAACUCGACUACAUACAC
90 20 70 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118
aspsirna0054 GUUUGAGCUAAUGUAUGUG
CAAACUCGAUUACAUACAC
34 23 11 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118
aspsirna0055 GUUUGAGCCGAUGUAUGUG
CAAACUCGGCUACAUACAC
32 30 2 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118
aspsirna0056 GUUUGAGCCAAUGUAUGUG
CAAACUCGGUUACAUACAC
0 22 -22 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118
aspsirna0057 GCUGAUGUAUGUGACGCUG
CGACUACAUACACUGCGAC
92 58 34 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118
aspsirna0058 GCUAAUGUAUGUGACGCUG
CGAUUACAUACACUGCGAC
92 58 34 HTT Huntington disease (HD) c.8163G>A,c.52CAG(36_39) rs2276881
19289118