ASPsiRNA ID | Pairing of target region (top) and ASP-siRNA (bottom) | Efficacy (mut)(%) | Efficacy (wt) (%) | Diff | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
---|---|---|---|---|---|---|---|---|---|---|
ASPsiRNA ID | Mutant allele/ASP-siRNA | Efficacy for mutant(%) |
Efficacy for wild (%) |
Relative Difference (%) | Gene | Disease | Mutation | RefSNP | Analysis | Pubmed ID |
aspsirna0053 | GUUUGAGCUGAUGUAUGUG CAAACUCGACUACAUACAC |
90 | 20 | 70 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 | ||
aspsirna0054 | GUUUGAGCUAAUGUAUGUG CAAACUCGAUUACAUACAC |
34 | 23 | 11 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 | ||
aspsirna0055 | GUUUGAGCCGAUGUAUGUG CAAACUCGGCUACAUACAC |
32 | 30 | 2 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 | ||
aspsirna0056 | GUUUGAGCCAAUGUAUGUG CAAACUCGGUUACAUACAC |
0 | 22 | -22 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 | ||
aspsirna0057 | GCUGAUGUAUGUGACGCUG CGACUACAUACACUGCGAC |
92 | 58 | 34 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 | ||
aspsirna0058 | GCUAAUGUAUGUGACGCUG CGAUUACAUACACUGCGAC |
92 | 58 | 34 | HTT | Huntington disease (HD) | c.8163G>A,c.52CAG(36_39) | rs2276881 |